Meet ApplyKite Twin, the application assistant that learns with you

Meet your Twin, it learns with you

Your Twin learns with you

Launch week codes:30% off annual Pro20% off monthly Pro

Ends in00h00m00s

Giuseppe Ronzitti

Researcher

INSERM

France

Research Interests

Explore related searches

Professors in France Professors in Tissue Engineering Tissue Engineering professors in France

Articles (20)

Year:

2026

Year:

2026

Year:

2026

Year:

2026

Year:

2026

Year:

2026

Year:

2025

Year:

2025

Year:

2025

Year:

2025

Year:

2025

Year:

2025

Year:

2025

Year:

2025

Year:

2024

Year:

2024

Year:

2024

Year:

2024

Year:

2024

Year:

2023

Collaborators (15)

Fatima Bosch

Catedrática de Universidad

Universitat Autònoma de Barcelona (UAB)

SPAIN

View details

Nicola Brunetti-Pierri

Professore Ordinario

Università degli Studi di Napoli Federico II

ITALY

View details

Roberta Caccia

San Raffaele Telethon Institute for Gene Therapy

ITALY

View details

Otto Baba

Professor

Tokushima University

JAPAN

View details

Julien Baruteau

Professor of Paediatric Metabolic Medicine

University College London

UNITED KINGDOM

View details

Catherine Vignal Clermont

Praticien attaché

Hôpital National des 15-20

FRANCE

View details

Fanny Collaud

Genethon (France)

FRANCE

View details

Angela Gritti

Assistant Professor of Human Histology

Vita-Salute San Raffaele University

ITALY

View details

Karen Louise Thomsen

DENMARK

View details

Deniz Dalkara

INSERM

FRANCE

View details

David Gross

INSERM

FRANCE

View details

Nico Mitro

Full Professor

Università degli Studi di Perugia Dipartimento di Scienze Farmaceutiche

ITALY

View details

Andrea Messina

Assistant Professor (Research Tenure-Track, RTT)

University of Trento

ITALY

View details

Stefano Gustincich

Principal Investigator - Tenured

Istituto Italiano di Tecnologia

ITALY

View details

Daniel Stone

Fred Hutchinson Cancer Research Center

UNITED STATES

View details

ApplyKite TwinLearns as you apply

Make your next move.

Prepare your application

Review drafts before you send them.

Giuseppe Ronzitti

Research Interests

Explore related searches

Articles (20)

Inter-individual variability in immune response to AAV ocular gene delivery across species impedes immunomonitoring

S-Nitrosylation of glycogen phosphorylase regulates nuclear glycogenolysis and is impaired in metabolic liver disorders.

Promises of co-stimulatory inhibition for durable and repeatable AAV gene therapy

Enhanced lysosomal glycogen breakdown is associated with liver tumorigenesis in glycogen storage disease type III

Identification of alterations of immunometabolism associated with Pompe disease

Imlifidase enables AAV gene therapy in a seropositive Crigler-Najjar patient: On the verge of a paradigm shift

AAV vectors trigger DNA damage response-dependent pro-inflammatory signalling in human iPSC-derived CNS models and mouse brain

SINEUP RNA rescues molecular phenotypes associated with CHD8 suppression in autism spectrum disorder model systems

Harnessing B19-directed CAR T cells for AAV vector administration in seropositive patients: The importance of the niche.

Advancing AAV technology: From capsid design to scalable manufacturing.

A myotropic AAV vector combined with skeletal muscle &lt;i&gt;cis&lt;/i&gt;-regulatory elements improve glycogen clearance in mouse models of Pompe disease.

Galectin-3: a novel biomarker of glycogen storage disease type III.

Rescue of lysosomal acid lipase deficiency in mice by rAAV8 liver gene transfer.

Liver fibrosis negatively impacts in vivo gene transfer to murine hepatocytes.

Synergism of dual AAV gene therapy and rapamycin rescues GSDIII phenotype in muscle and liver.

Repeated dosing of AAV-mediated liver gene therapy in juvenile rat and mouse models of Crigler-Najjar syndrome type I.

Predictive power of deleterious single amino acid changes to infer on AAV2 and AAV2-13 capsids fitness

271st ENMC international workshop: Towards a unifying effort to fight Kennedy's disease. 20-22 October 2023, Hoofddorp, Netherlands

A functional mini-GDE transgene corrects impairment in models of glycogen storage disease type III

Muscle-specific, liver-detargeted adeno-associated virus gene therapy rescues Pompe phenotype in adult and neonate Gaa<sup>-/-</sup> mice.

Collaborators (15)

Fatima Bosch

Nicola Brunetti-Pierri

Roberta Caccia

Otto Baba

Julien Baruteau

Catherine Vignal Clermont

Fanny Collaud

Angela Gritti

Karen Louise Thomsen

Deniz Dalkara

David Gross

Nico Mitro

Andrea Messina

Stefano Gustincich

Daniel Stone

Make your next move.

A myotropic AAV vector combined with skeletal muscle <i>cis</i>-regulatory elements improve glycogen clearance in mouse models of Pompe disease.